Antisense oligonucleotide splicing modulation as a novel Cystic Fibrosis therapeutic approach for the W1282X nonsense mutation

Yifat S. Oren, Ofra Avizur-Barchad, Efrat Ozeri-Galai, Renana Elgrabli, Meital R. Schirelman, Tehilla Blinder, Chava D. Stampfer, Merav Ordan, Onofrio Laselva, Malena Cohen-Cymberknoh, Eitan Kerem, Christine E. Bear, Batsheva Kerem*

*Corresponding author for this work

Research output: Contribution to journal › Article › peer-review

21 Scopus citations

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Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry

Neuroscience