Antisense oligonucleotide therapeutic approach for Timothy syndrome
- Xiaoyu Chen
- , Fikri Birey
- , Min Yin Li
- , Omer Revah
- , Rebecca Levy
- , Mayuri Vijay Thete
- , Noah Reis
- , Konstantin Kaganovsky
- , Massimo Onesto
- , Noriaki Sakai
- , Zuzana Hudacova
- , Jin Hao
- , Xiangling Meng
- , Seiji Nishino
- , John Huguenard
- , Sergiu P. Pașca*
*Corresponding author for this work
Research output: Contribution to journal › Article › peer-review
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