Neonatal gene therapy of glycogen storage disease type Ia using a feline immunodeficiency virus-based vector

Keyphrases

• Glucose-6-phosphatase (G6Pase) 100%
• Virus Vector 100%
• Feline Immunodeficiency Virus 100%
• Glycogen Storage Disease 100%
• Neonatal Gene Therapy 100%
• Blood Glucose 66%
• Illness 33%
• Gene Therapy 33%
• Murine Model 33%
• Disease Symptoms 33%
• Non-primate 33%
• Lentivirus 33%
• Long-term Transgene Expression 33%
• Glucose Homeostasis 33%
• Life-threatening Complications 33%
• Metabolic Disorders 33%
• Liver Glycogen 33%
• Wild Type Virus 33%
• Single Administration 33%
• Pathological Phenotype 33%
• Administration Regimen 33%
• Long-term Consequences 33%
• Murine Liver 33%
• Hepatocyte Cell Line 33%
• Neonatal Administration 33%
• Biochemical Phenotype 33%
• Normal Blood 33%
• Von Gierke Disease 33%

Immunology and Microbiology

• Feline Immunodeficiency Virus 100%
• Glucose Blood Level 66%
• Cell Line 33%
• Virus Type 33%
• Wild Type 33%
• Body Weight 33%
• Transgene 33%
• Lentivirus 33%
• Viral Vector 33%
• Glucose Homeostasis 33%
• Glycogen Liver Level 33%